Clinical trials in progress

Close up image of a male and female with their faces side by side

Information up-to-date as of February 2022

Although there are a number of LHON clinical trials ongoing around the world, there are none currently recruiting in the UK.

Trials that are currently recruiting in other countries include research into:

  • Gene therapy for the treatment of LHON with certain mutations
  • A treatment called bezafibrate (Befizal®) for the treatment of LHON
  • New techniques for looking at eye structure and function
  • Stem cell treatment

More trials may become available in the future. If you are interested in taking part in a trial, or just interested in what trials are happening, it is worth checking with a clinical trial registry such as You can click here to find more up-to-date details of current clinical trials in LHON that have been listed on this registry.